A look at clinical trials underway or in preparation in France and worldwide.
A look at clinical trials underway or in preparation in France and worldwide
Find out about clinical trials, observational studies and registers concerning neuromuscular diseases, in preparation or in progress.
The information comes mostly from the US site ClinicalTrials.gov. Presented according to disease or group of diseases, studies are classified into: - innovative biotherapies (gene therapy, cell therapy), - gene therapies, - pharmacotherapies (excluding pharmacogenetics), - observational studies, - other types of therapies (rehabilitation, medical devices).
Trials and treatments supported by AFM-Telethon
AFM-Telethon supports the development of therapies for rare genetic diseases, among which neuromusclar conditions, as well as clinical trials. Some treatments that have been supported by AFM-Telethon are now approved. More information about trials and treatments developed with our support