AFM-Telethon, Drew Weissman and James Dowling join forces to develop the next generation of gene therapies
AFM-Telethon is launching a two-year strategic research programme with Professor Drew Weissman, recipient of the 2023 Nobel Prize in Physiology or Medicine for his groundbreaking work on messenger RNA, and Professor James Dowling, a leading expert in neuromuscular diseases, at the University of Pennsylvania. The aim is to develop lipid nanoparticles capable of targeting muscle tissue while minimising uptake by the liver.








